Grant History

The $5.1M of total grant support we've given to funding research is made possible by the generosity of our sponsors and donors. Real people making an impact on saving children's eyesight.

Grant Amount

$3M
2024
$2.1M

2025

Year
Grant Amount
Month
Amount/ month
Purpose

2026

$1.1M

January
$1.1M

To close the remaining funding gap required to launch the AXV-101 clinical trial, enabling the study to begin in early 2026.

2025

$1M

September
$1M

To support clinical development of the first-in-human trial, including trial preparation and regulatory progress following clinical trial clearance.

2024

$3M

October
$1M
December
$2M

To fund the preclinical development and regulatory preparation of AXV-101, a gene therapy for Bardet-Biedl Syndrome type 1 (BBS1), advancing the program toward its first human clinical trial.

News and Articles

Recent News
January 06, 2026
A Race Against Blindness Awards Additional $1.1 Million Grant to Ensure Advancement of AXV-101 into Clinical Trial for Bardet-Biedl Syndrome 1 (BBS1)

Newly added funding closes critical gap and enables planned trial initiation in early 2026

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A Race Against Blindness Awards Additional $1.1 Million Grant to Ensure Advancement of AXV-101 into Clinical Trial for Bardet-Biedl Syndrome 1 (BBS1)

Latest Posts

September 19, 2025
New Hope for Retinitis Pigmentosa: FDA Grants Fast Track Designation for ADX-2191

FDA Fast Tracks Potential RP Treatment
Aldeyra’s ADX-2191 has received Fast Track Designation from the FDA for retinitis pigmentosa. With no approved treatments currently available for most RP patients, this milestone could help speed the development of a promising new therapy.

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September 15, 2025
Nanoscope Therapeutics Advances One-Time Gene Therapy for Retinitis Pigmentosa and Stargardt Disease

Hope for RP and Stargardt Disease
Nanoscope Therapeutics is advancing a one-time gene therapy designed to restore vision for patients with retinitis pigmentosa and Stargardt disease. If successful, this treatment could transform care for two conditions that currently have no approved therapies.

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September 15, 2025
Stem Cell–Derived Retinal Sheets Enter Clinical Trial for Retinitis Pigmentosa

Stem Cell–Derived Retinal Sheets Trial for RP
A new clinical trial is testing DSP-3077, a one-time stem cell–derived retinal sheet implant, as a potential treatment for retinitis pigmentosa. This regenerative therapy could offer hope for patients regardless of genetic subtype. Learn how this groundbreaking study may shape the future of RP treatment.

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Grant Announcements September 04, 2025
Celebrating a $1M Milestone for Sight-Saving Science
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September 01, 2025
Why We Run Multiple Fundraisers

Some wonder why we host several fundraisers each year. The answer is urgency: children with Bardet-Biedl Syndrome are losing vision every day. Running multiple campaigns helps us raise funds quickly, reach more people, and keep hope alive for sight-saving research.

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